In Viljem Julijan Association for Children with Rare Diseases we are on a mission to develop gene therapy for Cockayne syndrome – type B and we are raising funds to support research and development of gene therapy.

Our mission was initiated by 4-years old girl Karolina who has Cockayne syndrome – type B and with her parents we wish to save her life. We have partnered with two research groups in USA and Portugal, which are developing gene therapy for CSB.